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Lipidoses - 55 Studies Found
Estado | Estudiar |
Recruiting |
Nombre del estudio: International Registry Study of Neutral Lipid Storage Disease (NLSD) / Triglyceride Deposit Cardiomyovasculopathy (TGCV) and Related Diseases Condición: Neutral Lipid Storage Disease Fecha: 2016-08-04 |
Completed |
Nombre del estudio: The Effect of Fibrate Therapy in Two Patients With Neutral Lipid Storage Disease With Myopathy (NLSDM) Condición: Neutral Lipid Storage Disease Fecha: 2012-01-16 Intervenciones: Drug: Fibrate treatment Patients will receive a dosage of 400mg Bezafibrate every day during 28 weeks |
Recruiting |
Nombre del estudio: Safety, Tolerability, PK, and Efficacy Evaluation of Repeat Ascending Doses of Olipudase Alfa in Pediatric Patients <18 Years of Age With Acid Sphingomyelinase Deficiency Condición: Sphingomyelin Lipidosis Fecha: 2014-11-07 Intervenciones: Drug: Olipudase alfa Pharmaceutical form: powder for concentrate for solution for infusion Route of admi |
Recruiting |
Nombre del estudio: A Long-Term Study of Olipudase Alfa in Patients With Acid Sphingomyelinase Deficiency Condición: Sphingomyelin Lipidosis Fecha: 2013-11-26 Intervenciones: Drug: GZ402665 Pharmaceutical form: Powder for concentrate |
Recruiting |
Nombre del estudio: Efficacy, Safety, Pharmacodynamic, and Pharmacokinetics Study of Olipudase Alfa in Patients With Acid Sphingomyelinase Deficiency Condición: Sphingomyelin Lipidosis Fecha: 2013-11-26 Intervenciones:
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Recruiting |
Nombre del estudio: Clinical Study on the Safety of CNT-02 for TGCV and NLSD-M Condición:
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Recruiting |
Nombre del estudio: Study of Inborn Errors of Cholesterol Synthesis and Related Disorders Condición: Lipoidosis Fecha: 2002-09-21 |
Completed |
Nombre del estudio: SCH-58235 (Ezetimibe) to Treat Homozygous Sitosterolemia Condición: Lipoidosis Fecha: 2002-09-10 Intervenciones: Drug: SCH-58235 |
Recruiting |
Nombre del estudio: International Collaborative Gaucher Group (ICGG) Gaucher Registry Condición:
Intervenciones: Drug: Cerezyme (imiglucerase for injection) |