Lipidoses - 55 Studies Found
Terminated |
: Natural History Study of Children With Metachromatic Leukodystrophy :
: 2010-01-05 : |
Completed |
: Phase I Study of Retrovirally Mediated Transfer of the Human Glucocerebrosidase Gene Into Peripheral Blood Stem Cells for Autologous Transplantation in Patients With Type I Gaucher Disease : Gaucher's Disease : 1999-10-18 : Genetic: human glucocerebrosidase gene into autologous peripheral blood stem cells |
Completed |
: Phase II Study of Glucocerebrosidase in Patients With Gaucher Disease : Gaucher's Disease : 1999-10-18 : Drug: glucocerebrosidase |
Completed |
: Phase II Randomized Study of Alendronate Sodium for Osteopenia in Patients With Gaucher's Disease :
: 1999-10-18 :
|
Recruiting |
: Krabbe Disease Global Patient Registry : Krabbe Disease : 2016-12-06 |
Completed |
: Study to Evaluate Blood Cell Lines From Patients With Gaucher Disease : Gaucher Disease : 2006-07-10 : Procedure: Blood sample |
Recruiting |
: Biomarker for Krabbe Disease :
: 2011-08-29 |
Recruiting |
: Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation :
|
Completed |
: Stem Cell Transplantation (SCT) for Genetic Diseases :
|